An in-person conversation at the 2025 Connecticut Rare Disease Forum with The National Organization for Rare Disorder’s President/CEO Pam Gavin sharing how patient advocacy organizations are vital to research and development.
All tagged nano rare diseases
#322 Susannah’s Nano-Rare Journey: 2 Years of Treatment and Triumph
Join Susannah’s father, Luke Rosen, and her physician, Dr. Jennifer Bain, as they share her remarkable progress and hope-filled journey with n-Lorem’s groundbreaking nano-rare treatments.
#274 Wolfram Syndrome with Stephanie Snow Gebel
Episode drop of “It Happened To Me” focusing on the rare disease Wolfram Syndrome.
#219 It Happened To Me Podcast: Genetic Counselors for Rare Diseases
Episode drop of “It Happened To Me” with Kira Dineen sharing how genetic counselors can help people with rare diseases.